02.18.26 -- Policy Matters: The Reauthorized Rare Pediatric Disease Voucher Program

Hear how one family, driven by urgency, partnered with AAV experts to develop a treatment for their daughter’s ultra-rare neurodegenerative disorder, NEDAMSS, in just 14 months.

Bridge the enrollment gap by blending site-based tactics with global direct-to-patient outreach. Use digital screening and EMR intelligence to ensure faster, more predictable paths to randomization.

Data quality and governance underpin portfolio, clinical trial, and commercial decisions. Combined with trustworthy, explainable AI, they enable complete insights for optimization, feasibility, forecasting, and planning.

The first oral GLP‑1 therapy for obesity delivers notable weight‑loss and cardiovascular benefits. This breakthrough offers a convenient new option for patients and providers managing obesity.

For over 20 years, teams have supported biotech and pharma groups in validating and launching new or renovated facilities. A flexible, integrated model enables smooth collaboration and long‑term success.

Advances in technology have expanded the use of fermentation across many applications. Explore how synthetic biology and supporting innovations are shaping modern fermentation practices.